Genetic eye disease
SCIE.11.137
THERAPEUTIC HOMOLOGY-INDEPENDENT TARGETED INTEGRATION IN RETINA AND LIVER

Esposito F. * [1] , Dell'Aquila F. [1] , Ferla R. [1] , Padmanaban A. [1] , Lupo M. [1] , Llado M. [1] , Tornabene P. [1] , Sureda Horrach P. [1] , Auricchio S. [1] , Marrocco E. [1] , Dell'Anno M. [1] , Nusco E. [1] , Trapani I. [1] , Surace E.M. [2] , Manfredi A. [2] , Di Filippo L. [1] , Torella A. [1] , Peluso G. [1] , Cacchiarelli D. [1] , Nigro V. [1] , Auricchio A. [3]

Pozzuoli [1] , Napoli [2] , Naples [3]
SCIE.05.138
UBIAD1 AND FERROPTOSIS: EXPLORING A CURE FOR SCHNYDER CORNEAL DYSTROPHY (SCD)

Tosi G. [1] , Lugato P. [1] , Simonato M. [2] , Cogo P. [2] , Santoro M. * [1]

Padova [1] , Udine [2]
SCIE.11.139
MUTATION-INDEPENDENT GENOME EDITING APPROACHES FOR TREATMENT OF STARGARDT DISEASE

Pugni E. , Tenderini E. , Cascone A. , Razzano F. , Mazzaro N. , Lupo M. , Casciello M. , Marrocco E. , Trapani I. *

Pozzuoli
SCIE.11.133
MIR-181A/B DOWNREGULATION: A MUTATION-INDEPENDENT THERAPEUTIC APPROACH FOR INHERITED RETINAL DISEASES

Di Guida M. [1] , Petrogiannakis G. [1] , Capasso D. [1] , Brandi P. [1] , Garcia-Piqueras J. [1] , Ruiz-Ceja K.A. [1] , Negueruela S. [1] , Pizzo M. [1] , Capolongo F. [1] , Karali M. [2] , Franco B. [1] , Indrieri A. [1] , Carrella S. [1] , Banfi S. * [1]

Pozzuoli (NA) [1] , Naples [2]
SCIE.11.135
PIGMENT EPITHELIUM-DERIVED FACTOR (PEDF) AND DERIVED PEPTIDES AS THERAPEUTIC AGENTS FOR INHERITED RETINAL DEGENERATION

Bighinati A. [1] , Adani E. [1] , Piano I. [2] , Gargini M.C. [2] , Ottonelli I. [1] , Tosi G. [1] , Becerra S.P. [3] , Marigo V. * [1]

Modena [1] , Pisa [2] , Bethesda [3]
SCIE.11.136
MODULATING AUTOPHAGY: A NOVEL GENE-INDEPENDENT THERAPEUTIC TREATMENT FOR ADRP

Intartaglia D. * [1] , Giamundo G. [2] , Salierno F. [1] , Conte I. [1]

Pozzuoli (Naples) [1] , Napoli [2]
SCIE.11.134
IDENTIFICATION OF DRUGS FOR AUTOSOMAL DOMINANT OPTIC ATROPHY (ADOA): FROM ADOA RCGS MODELS TO MICROPARTICLE-BASED DRUG DELIVERY IN AN ADOA MOUSE MODEL

Lacombe A. * , Mendonca A.P. , Rampado R. , Caliceti P. , Salmaso S. , Scorrano L.

Padova