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Genetic respiratory disease
SCIE.05.172
RESCUE OF MUTANT CFTR CHLORIDE CHANNELS BY A MIMETIC PEPTIDE TARGETING THE A-KINASE ANCHORING FUNCTION OF PI3KG

Della Sala A. * [1] , Murabito A. [1] , Mergiotti M. [1] , Capurro V. [2] , Loffreda A. [3] , Conti J. [4] , Raimondi A. [3] , Sondo E. [2] , Melotti P. [4] , Sorio C. [4] , Tacchetti C. [3] , Lukacs G. [5] , Pedemonte N. [2] , Hirsch E. [1] , Ghigo A. [1]

Torino [1] , Genova [2] , Milano [3] , Verona [4] , Montréal, Quebec [5]
SCIE.16.173
PHARMACOLOGICAL MODULATION OF ION TRANSPORT TO TREAT THE BASIC DEFECT IN CYSTIC FIBROSIS

Venturini A. , Borrelli A. , Genovese M. * , Guidone D. , Buccirossi M. , Renda M. , Galietta L.J.V.

Pozzuoli
SCIE.11.174
CRISPR/CAS-MEDIATED BASE EDITING: A PROMISING TOOL FOR DISEASE MODELING AND PERSONALIZED MEDICINE APPROACHES FOR PRIMARY CILIARY DYSKINESIA

Gabellini C. * , Lai M. , Perotti I. , De Carli A. , Maj D. , Erica Lucia C. , Pistello M. , Pifferi M.

Pisa