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Genetic neurological disorder\Polyneuropathies
SCIE.11.106
BOOSTING HSPB3 TO PREVENT NEUROMUSCULAR DEGENERATION IN PERIPHERAL NEUROPATHIES

Carra S. *

Modena
SCIE.05.107
KNOCKDOWN AND REPLACEMENT OF MFN2: A GENE THERAPY TO TREAT DOMINANTLY INHERITED PERIPHERAL NEUROPATHY CMT2A

Rizzo F. [1] , Abati E. [1] , Bono S. [1] , Ruepp M.D. [2] , Salani S. [1] , Ottoboni L. [1] , Melzi V. [1] , Cordiglieri C. [1] , Pagliarani S. [1] , De Gioia R. [1] , Anastasia A. [1] , Taiana M. [1] , Garbellini M. [1] , Lodato S. [1] , Kunderfranco P. [1] , Cazzato D. [1] , Cartelli D. [1] , Lonati C. [1] , Bresolin N. [1] , Comi G. [1] , Nizzardo M. [1] , Corti S. * [1]

Milan [1] , London [2]
SCIE.05.105
PHARMACOLOGICAL MODULATION OF MYELIN SYNTHESIS AND CYTOSKELETAL REMODELLING AS A THERAPEUTIC STRATEGY FOR CMT4B NEUROPATHIES WITH ABERRANT MYELIN

Rebuffini P. , Di Guardo R. , Cipriani S. , Bolino A. *

Milano
SCIE.11.104
MECHANISMS OF AXONAL DEGENERATION IN LATE ONSET CMT1B NEUROPATHIES: MOLECULAR PATHWAYS AND THERAPEUTIC APPROACHES

Claessens A. [1] , Shackleford G.G. [1] , De Blasis R. [1] , Ferri C. [1] , Baldi R. [1] , Valenzano S. [1] , Del Carro U. [1] , Crivellari L. [1] , Pisciotta C. [1] , Saveri P. [1] , Feltri L. [2] , Wrabetz L. [2] , Pareyson D. [1] , D'Antonio M. * [1]

Milan [1] , Buffalo [2]