SCIE.16.87
MENINGES AS AN OVERLOOKED PHARMACOLOGICAL TARGET FOR GLOBOID CELL LEUKODYSTROPHY
SCIE.16.88
IN VITRO VALIDATION OF LENTIVIRAL VECTORS ENCODING FOR CHIMERIC MURINE AND HUMAN GALC ENZYMES TO IMPROVE THE EFFICACY OF GENE THERAPY APPROACHES FOR GLOBOID CELL LEUKODYSTROPHY