Nuclease-free targeted integration of a promoter-less mini-ATP7B confers proliferative advantage to edited hepatocytes and corrects Wilson disease
Padula A. ,
Spinelli M. ,
Nusco E. ,
Capolongo F. ,
Campione S. ,
Perna C. ,
Bastille A. ,
Ericson M. ,
Wang C. ,
Zippo A. ,
Amoresano A. ,
Nacht M. ,
Piccolo P. *