SCIE.05.28
DISSECTING INNATE IMMUNITY AND NUCLEIC ACID SENSING IN GENE THERAPY AND DISEASE
SCIE.16.88
IN VITRO VALIDATION OF LENTIVIRAL VECTORS ENCODING FOR CHIMERIC MURINE AND HUMAN GALC ENZYMES TO IMPROVE THE EFFICACY OF GENE THERAPY APPROACHES FOR GLOBOID CELL LEUKODYSTROPHY