SCIE.05.3
NATURAL HISTORY OF BECKER MUSCULAR DYSTROPHY: TOWARD TRIAL READINESS
SCIE.05.5
DISTROFIA MUSCOLARE DI DUCHENNE: CORRELAZIONE GENOTIPO-FENOTIPO
SCIE.05.7
CHARACTERIZATION OF THE PHENOTYPIC DIVERSITY IN DUPEX2 DUCHENNE MUSCULAR DYSTROPHY AND IDENTIFICATION OF PREDICTIVE/PROGNOSTIC MARKERS
SCIE.05.18
TRIAL READINESS AND ENDPOINT ASSESSMENT IN CONGENITAL AND CHILDHOOD MYOTONIC DYSTROPHY: OUTCOME MEASURES AND ENDPOINT ASSESSMENTS (GUP19002)