SCIE.05.191
BONE DEFECTS AND CROSS-CORRECTION IN MPSIH HSPC-GT
SCIE.11.114
EX VIVO EXPANSION OF HEMATOPOIETIC STEM AND PROGENITOR CELLS (HSPC) FOR GENE THERAPY
SCIE.11.156
HUMAN HEMATOPOIETIC STEM/PROGENITOR CELL TRAFFICKING AND CLONAL TRACKING
SCIE.11.157
DECONVOLUTING THE DYNAMICS OF HEMATOPOIETIC RECONSTITUTION IN GENE THERAPY PATIENTS
SCIE.11.196
AN INNOVATIVE PLATFORM APPROACH FOR THE DEVELOPMENT OF EX-VIVO GENE THERAPIES FOR THE TREATMENT OF LYSOSOMAL STORAGE DISEASES WITH SKELETAL INVOLVEMENT