SCIE.05.28
DISSECTING INNATE IMMUNITY AND NUCLEIC ACID SENSING IN GENE THERAPY AND DISEASE
SCIE.05.158
AGE OF ADMINISTRATION IMPACTS THE EFFICIENCY OF LENTIVIRAL VECTOR-MEDIATED HEPATOCYTE TRANSDUCTION IN VIVO AND ITS DISTRIBUTION IN THE LIVER LOBULE
SCIE.11.48
DEVELOPMENT OF AN ALLELE-SPECIFIC EPIGENETIC SILENCING PLATFORM FOR THE TREATMENT OF SCA2
SCIE.11.156
HUMAN HEMATOPOIETIC STEM/PROGENITOR CELL TRAFFICKING AND CLONAL TRACKING
SCIE.16.115
ELUCIDATING THE SIGNIFICANCE OF OSTEOPETROTIC BONE MARROW NICHE IN HEMATOPOIETIC STEM AND PROGENITOR CELLS, AND ITS IMPLICATIONS FOR STEM CELL THERAPY