SCIE.11.36
THERAPEUTIC EFFICACY OF MIR-181A/B DOWN REGULATION IN LEIGH SYNDROME
SCIE.11.39
AAV-MEDIATED INHIBITION OF MIR-181A/B AS GENE-INDEPENDENT THERAPEUTIC TOOL FOR MITOCHONDRIAL DISEASES
SCIE.11.133
MIR-181A/B DOWNREGULATION: A MUTATION-INDEPENDENT THERAPEUTIC APPROACH FOR INHERITED RETINAL DISEASES