SCIE.05.197
A PRO-INFLAMMATORY SIGNATURE IN PATIENTS WITH LYSOSOMAL STORAGE DISORDERS DOES NOT PREVENT THE INDUCTION OF OF TOLEROGENIC CELLS TO PREVENT UNWONTED IMMUNE RESPONSES IN ENZYME REPLACEMENT THERAPY.
SCIE.11.194
EARLY DEVELOPMENT OF MPS-IIIA DOPAMINERGIC NEURONS: AT THE NEXUS OF BEHAVIOR CHANGES AND THERAPY